Two donors make Ted’s intervention in Poland possible

It has been possible yet again, this time with the help of two donors. They would like to remain anonymous as…

Marta is a four and a half year old girl with Niemann Pick C. This is a rare neurodegenerative genetic disease…

During the second term of 2019, we have followed and supported six new patients with their fight against cancer. They have…

Four year old Irai had a rare disease that only affected around 130 children worldwide: the aromatic amino acids de carboxylase…

4-year-old Irai will be the first Spanish patient to receive gene therapy treatment to cure her rare disease which prevents her…