{"id":18762,"date":"2026-03-26T14:05:27","date_gmt":"2026-03-26T13:05:27","guid":{"rendered":"https:\/\/fundacioncolumbus.org\/what-we-do\/"},"modified":"2026-10-07T09:16:06","modified_gmt":"2026-10-07T07:16:06","slug":"what-we-do","status":"publish","type":"page","link":"https:\/\/fundacioncolumbus.org\/en\/what-we-do\/","title":{"rendered":"What we do"},"content":{"rendered":"\t\t<div data-elementor-type=\"wp-page\" data-elementor-id=\"18762\" class=\"elementor elementor-18762 elementor-37\" data-elementor-post-type=\"page\">\n\t\t\t\t<div class=\"elementor-element elementor-element-ba5f58c e-flex e-con-boxed e-con e-parent\" data-id=\"ba5f58c\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t\t<div class=\"e-con-inner\">\n\t\t<div class=\"elementor-element elementor-element-e85e1e3 e-con-full e-flex e-con e-child\" data-id=\"e85e1e3\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-cbd052d elementor-widget-tablet__width-initial elementor-widget elementor-widget-heading\" data-id=\"cbd052d\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h1 class=\"elementor-heading-title elementor-size-default\">Accelerating access to advanced therapies for children with ultra-rare diseases<\/h1>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-6844a3e elementor-widget elementor-widget-heading\" data-id=\"6844a3e\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">Our vision: no child left without treatment<\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-1d9753b elementor-widget elementor-widget-text-editor\" data-id=\"1d9753b\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Treating an ultra-rare disease takes more than science. It takes coordination, sustained funding, strategic partnerships, and the involvement of society as a whole. <\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-36e8e3e e-con-full e-flex e-con e-child\" data-id=\"36e8e3e\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-529d0df elementor-widget elementor-widget-button\" data-id=\"529d0df\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"#salud\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">People<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-5e16b90 elementor-widget elementor-widget-button\" data-id=\"5e16b90\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"#innovacion\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Innovation<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-51dbd8f elementor-widget elementor-widget-button\" data-id=\"51dbd8f\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"#cultura\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Culture<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-ae0c26a e-flex e-con-boxed e-con e-parent\" data-id=\"ae0c26a\" data-element_type=\"container\" data-e-type=\"container\" id=\"salud\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t\t<div class=\"e-con-inner\">\n\t\t\t\t<div class=\"elementor-element elementor-element-b32d5b9 elementor-widget elementor-widget-heading\" data-id=\"b32d5b9\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">PEOPLE<\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-6b61e79 elementor-widget__width-initial elementor-widget elementor-widget-heading\" data-id=\"6b61e79\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h2 class=\"elementor-heading-title elementor-size-default\">Advanced therapies for those who need them most<\/h2>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-65c3da8 elementor-widget__width-initial elementor-widget elementor-widget-text-editor\" data-id=\"65c3da8\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>The burden of missing treatments for rare diseases falls on children and their families. Around the world, some parents and researchers have developed therapies for their own children, yet the real challenge is making that same therapy accessible to every other child with the same disease, without a company behind it. <\/p><p> <\/p><p>At Fundaci\u00f3n Columbus, we believe that if science has an answer, no child should be left without access to it. Every program we support, every family we accompany, and every treatment we make possible share one goal: to transform lives. <\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-175b172 e-con-full e-flex e-con e-child\" data-id=\"175b172\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-06ba539 e-con-full e-flex e-con e-child\" data-id=\"06ba539\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-26ee51c elementor-widget elementor-widget-heading\" data-id=\"26ee51c\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>+<\/span><span>55<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-58b9063 elementor-widget elementor-widget-text-editor\" data-id=\"58b9063\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">Children treated with gene therapy<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-a2132f1 e-con-full e-flex e-con e-child\" data-id=\"a2132f1\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-f31c6dd elementor-widget elementor-widget-heading\" data-id=\"f31c6dd\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>5<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-a6416d5 elementor-widget elementor-widget-text-editor\" data-id=\"a6416d5\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">Active research programs in development<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-fd773a6 e-con-full e-flex e-con e-child\" data-id=\"fd773a6\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-3bbb575 elementor-widget elementor-widget-heading\" data-id=\"3bbb575\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>3<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-46ebe7e elementor-widget elementor-widget-text-editor\" data-id=\"46ebe7e\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">Clinical trials in Europe: SPG50, CLN7, and CTNNB1<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-d5a126b elementor-align-center elementor-widget elementor-widget-button\" data-id=\"d5a126b\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"#objetivo10\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Explore our programs<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-1e35aed elementor-widget elementor-widget-heading\" data-id=\"1e35aed\" data-element_type=\"widget\" data-e-type=\"widget\" id=\"innovacion\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">INNOVATION<\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-d3e45a8 elementor-widget__width-initial elementor-widget elementor-widget-heading\" data-id=\"d3e45a8\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h2 class=\"elementor-heading-title elementor-size-default\">Gene therapy: addressing the root of the problem<\/h2>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-08cbffa elementor-widget__width-initial elementor-widget elementor-widget-text-editor\" data-id=\"08cbffa\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Many ultra-rare diseases originate from a single gene that isn&#8217;t working properly. Gene therapy introduces, replaces, or silences that gene in the patient&#8217;s cells, giving it the instructions it needs to function correctly. It doesn&#8217;t treat the symptoms: it targets the cause. <\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-7eeec37 e-con-full e-flex e-con e-child\" data-id=\"7eeec37\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-bbb5645 e-con-full e-flex e-con e-child\" data-id=\"bbb5645\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-cfe3b57 elementor-widget elementor-widget-image\" data-id=\"cfe3b57\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<img fetchpriority=\"high\" decoding=\"async\" width=\"195\" height=\"279\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/ICONO-TERAPIA-GENICA-P288-1.svg\" class=\"attachment-large size-large wp-image-18774\" alt=\"\" \/>\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-5672afd elementor-widget elementor-widget-text-editor\" data-id=\"5672afd\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">A defective gene causes the disease<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-e3f8500 elementor-widget__width-initial e-transform elementor-widget elementor-widget-image\" data-id=\"e3f8500\" data-element_type=\"widget\" data-e-type=\"widget\" data-settings=\"{&quot;_transform_rotateZ_effect_mobile&quot;:{&quot;unit&quot;:&quot;deg&quot;,&quot;size&quot;:90,&quot;sizes&quot;:[]},&quot;_transform_rotateZ_effect&quot;:{&quot;unit&quot;:&quot;px&quot;,&quot;size&quot;:&quot;&quot;,&quot;sizes&quot;:[]},&quot;_transform_rotateZ_effect_tablet_extra&quot;:{&quot;unit&quot;:&quot;deg&quot;,&quot;size&quot;:&quot;&quot;,&quot;sizes&quot;:[]},&quot;_transform_rotateZ_effect_tablet&quot;:{&quot;unit&quot;:&quot;deg&quot;,&quot;size&quot;:&quot;&quot;,&quot;sizes&quot;:[]}}\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<img decoding=\"async\" width=\"315\" height=\"258\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/03\/Flecha-Azul.svg\" class=\"attachment-large size-large wp-image-18775\" alt=\"\" \/>\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-7d5d250 e-con-full e-flex e-con e-child\" data-id=\"7d5d250\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-4bcfd31 elementor-widget elementor-widget-image\" data-id=\"4bcfd31\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<img decoding=\"async\" width=\"301\" height=\"279\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/ICONO-TERAPIA-GENICA-P288-2.svg\" class=\"attachment-large size-large wp-image-18776\" alt=\"\" \/>\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-33969a1 elementor-widget elementor-widget-text-editor\" data-id=\"33969a1\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">The vector delivers an edited gene<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-68d3b6c e-transform elementor-widget-tablet__width-initial elementor-widget elementor-widget-image\" data-id=\"68d3b6c\" data-element_type=\"widget\" data-e-type=\"widget\" data-settings=\"{&quot;_transform_rotateZ_effect_mobile&quot;:{&quot;unit&quot;:&quot;deg&quot;,&quot;size&quot;:90,&quot;sizes&quot;:[]},&quot;_transform_rotateZ_effect&quot;:{&quot;unit&quot;:&quot;px&quot;,&quot;size&quot;:&quot;&quot;,&quot;sizes&quot;:[]},&quot;_transform_rotateZ_effect_tablet_extra&quot;:{&quot;unit&quot;:&quot;deg&quot;,&quot;size&quot;:&quot;&quot;,&quot;sizes&quot;:[]},&quot;_transform_rotateZ_effect_tablet&quot;:{&quot;unit&quot;:&quot;deg&quot;,&quot;size&quot;:&quot;&quot;,&quot;sizes&quot;:[]}}\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<img decoding=\"async\" width=\"315\" height=\"258\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/03\/Flecha-Azul.svg\" class=\"attachment-large size-large wp-image-18775\" alt=\"\" \/>\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-3f4f758 e-con-full e-flex e-con e-child\" data-id=\"3f4f758\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-a7f5295 elementor-widget elementor-widget-image\" data-id=\"a7f5295\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"230\" height=\"283\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/ICONO-TERAPIA-GENICA-P288-3.svg\" class=\"attachment-large size-large wp-image-18777\" alt=\"\" \/>\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-f71a6b0 elementor-widget elementor-widget-text-editor\" data-id=\"f71a6b0\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">The cell repairs itself, improving the patient&#8217;s life<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-b5ef63c e-con-full e-flex e-con e-child\" data-id=\"b5ef63c\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-832062c elementor-widget elementor-widget-text-editor\" data-id=\"832062c\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p><span style=\"font-weight: 400;\">Are you a physician, researcher, or institution?<\/span><br><a href=\"https:\/\/fundacioncolumbus.org\/en\/contact\/\"><span style=\"font-weight: 800;\">Request the technical details of our programs<\/span><\/a><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-c5874a0 elementor-widget elementor-widget-image\" data-id=\"c5874a0\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<a href=\"https:\/\/fundacioncolumbus.org\/en\/contact\/\">\n\t\t\t\t\t\t\t<img decoding=\"async\" width=\"315\" height=\"258\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/03\/Flecha-Azul.svg\" class=\"attachment-large size-large wp-image-18775\" alt=\"\" \/>\t\t\t\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-57b800a e-flex e-con-boxed e-con e-parent\" data-id=\"57b800a\" data-element_type=\"container\" data-e-type=\"container\" id=\"objetivo10\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t\t<div class=\"e-con-inner\">\n\t\t\t\t<div class=\"elementor-element elementor-element-c614fcd elementor-widget elementor-widget-heading\" data-id=\"c614fcd\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">Goal 10<\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-3bf8952 elementor-widget elementor-widget-heading\" data-id=\"3bf8952\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h2 class=\"elementor-heading-title elementor-size-default\">10 ultra-rare diseases<br \/>10 effective treatments <br \/><br \/><\/h2>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-be628cc elementor-widget elementor-widget-text-editor\" data-id=\"be628cc\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Today, we&#8217;re working on five active programs. Each one represents years of research, scientific partnerships, and families who refused to give up. Our goal is to develop 10 effective treatments for 10 ultra-rare diseases.  <\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-789b4d5 e-con-full e-flex e-con e-child\" data-id=\"789b4d5\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-6a41b33 e-con-full e-flex e-con e-child\" data-id=\"6a41b33\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-7173563 e-con-full e-flex e-con e-child\" data-id=\"7173563\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-9bc37ee fcol-tab is-active elementor-tablet-align-center elementor-widget-tablet__width-inherit elementor-widget-mobile__width-inherit elementor-widget elementor-widget-button\" data-id=\"9bc37ee\" data-element_type=\"widget\" data-e-type=\"widget\" data-tab=\"aadc\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"#\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">AADC<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-8a20f6d e-con-full e-flex e-con e-child\" data-id=\"8a20f6d\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-8c70b09 fcol-tab elementor-widget-mobile__width-inherit elementor-tablet-align-center elementor-widget-tablet__width-inherit elementor-widget elementor-widget-button\" data-id=\"8c70b09\" data-element_type=\"widget\" data-e-type=\"widget\" data-tab=\"spg50\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"#\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">SPG50<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-68ac2b7 e-con-full e-flex e-con e-child\" data-id=\"68ac2b7\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-6b7b0fe fcol-tab elementor-tablet-align-center elementor-widget-tablet__width-inherit elementor-widget-mobile__width-inherit elementor-widget elementor-widget-button\" data-id=\"6b7b0fe\" data-element_type=\"widget\" data-e-type=\"widget\" data-tab=\"ctnnb1\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"#\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">CTNNB1<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-e0142b8 e-con-full e-flex e-con e-child\" data-id=\"e0142b8\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-7ff5722 fcol-tab elementor-tablet-align-center elementor-widget-tablet__width-inherit elementor-widget-mobile__width-inherit elementor-widget elementor-widget-button\" data-id=\"7ff5722\" data-element_type=\"widget\" data-e-type=\"widget\" data-tab=\"cmt4j\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"#\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">CMT4J<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-67f7fa0 e-con-full e-flex e-con e-child\" data-id=\"67f7fa0\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-b443427 fcol-tab elementor-tablet-align-center elementor-widget-tablet__width-inherit elementor-widget-mobile__width-inherit elementor-widget elementor-widget-button\" data-id=\"b443427\" data-element_type=\"widget\" data-e-type=\"widget\" data-tab=\"cln7\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"#\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">CLN7<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-4d6b311 e-con-full e-flex e-con e-child\" data-id=\"4d6b311\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-58f5eec fcol-tab elementor-align-center elementor-widget__width-inherit elementor-widget-tablet__width-inherit elementor-widget-mobile__width-inherit elementor-widget elementor-widget-button\" data-id=\"58f5eec\" data-element_type=\"widget\" data-e-type=\"widget\" data-tab=\"more\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"#\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">+<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-5ba34c3 e-con-full fcol-panels e-flex e-con e-child\" data-id=\"5ba34c3\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t<div class=\"elementor-element elementor-element-0e9eea7 e-con-full fcol-panel is-active e-flex e-con e-child\" data-id=\"0e9eea7\" data-element_type=\"container\" data-e-type=\"container\" id=\"aadc\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-3f8a16d elementor-widget elementor-widget-heading\" data-id=\"3f8a16d\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h3 class=\"elementor-heading-title elementor-size-default\">Aromatic L-amino acid<br \/>decarboxylase deficiency <br \/><br \/><\/h3>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-fc29f31 elementor-widget elementor-widget-heading\" data-id=\"fc29f31\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">Gene therapy using an AAV2 vector carrying the AADC gene<\/p>\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-11334cc e-con-full e-flex e-con e-child\" data-id=\"11334cc\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-7433cf6 e-con-full e-flex e-con e-child\" data-id=\"7433cf6\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-45562ce elementor-widget elementor-widget-heading\" data-id=\"45562ce\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">Phase I\/II<\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-cdebaa5 elementor-widget elementor-widget-text-editor\" data-id=\"cdebaa5\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>In the U.S.<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-74699d7 e-con-full e-flex e-con e-child\" data-id=\"74699d7\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-ddab11c elementor-widget elementor-widget-heading\" data-id=\"ddab11c\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<span class=\"elementor-heading-title elementor-size-default\">Dr. Krystof Bankiewicz<\/span>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-c31818b elementor-widget elementor-widget-text-editor\" data-id=\"c31818b\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Program lead<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-4a0dff0 e-con-full e-flex e-con e-child\" data-id=\"4a0dff0\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-5f3dc49 elementor-widget elementor-widget-heading\" data-id=\"5f3dc49\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>32<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-7715f8d elementor-widget elementor-widget-text-editor\" data-id=\"7715f8d\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>children treated<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-18ba9a7 e-con-full e-flex e-con e-child\" data-id=\"18ba9a7\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-48aaa74 elementor-widget elementor-widget-text-editor\" data-id=\"48aaa74\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p><span class=\"TextRun SCXW178276474 BCX0\" lang=\"ES-ES\" data-contrast=\"auto\">AADC is an inherited neurological disorder that prevents the brain from producing dopamine and serotonin, causing developmental delay, low muscle tone, spasms, and loss of motor control from the first year of life. Gene therapy delivers a functional copy of the defective gene directly into brain cells, with remarkable results: improved head control, fewer involuntary movements, and, in many cases, the recovery of speech and walking. This was the first disease we treated, led by Dr. Bankiewicz, a world-renowned expert in neurorestorative medicine and Professor of Neurological Surgery at UCSF.<\/span><span class=\"LineBreakBlob BlobObject DragDrop SCXW178276474 BCX0\"><span class=\"SCXW178276474 BCX0\"> <\/span><\/span><\/p><p><span class=\"LineBreakBlob BlobObject DragDrop SCXW178276474 BCX0\"><span class=\"SCXW178276474 BCX0\">*This program is currently available only in the United States. Contact <a href=\"mailto:info@fundacioncolumbus.org\">info@fundacioncolumbus.org<\/a> for more information about the project. <\/span><br class=\"SCXW178276474 BCX0\"><\/span><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-592d10d e-con-full e-flex e-con e-child\" data-id=\"592d10d\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-5cedea6 elementor-align-center elementor-mobile-align-left elementor-widget-mobile__width-inherit elementor-widget elementor-widget-button\" data-id=\"5cedea6\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/real-stories\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Discover real stories<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-ede933c elementor-align-center elementor-mobile-align-left elementor-widget elementor-widget-button\" data-id=\"ede933c\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/donate\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Support us<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-e4b8da2 elementor-widget elementor-widget-text-editor\" data-id=\"e4b8da2\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p><span class=\"LineBreakBlob BlobObject DragDrop SCXW178276474 BCX0\"><span class=\"TextRun SCXW87226098 BCX0\" lang=\"EN-US\" data-contrast=\"auto\"><span class=\"NormalTextRun SCXW87226098 BCX0\">Source: <\/span><\/span><a class=\"Hyperlink SCXW87226098 BCX0\" href=\"https:\/\/pubmed.ncbi.nlm.nih.gov\/34253733\/\" target=\"_blank\" rel=\"noreferrer noopener\"><span class=\"TextRun Underlined SCXW87226098 BCX0\" lang=\"EN-US\" data-contrast=\"none\"><span class=\"NormalTextRun SCXW87226098 BCX0\" data-ccp-charstyle=\"Hyperlink\">https:\/\/pubmed.ncbi.nlm.nih.gov\/34253733\/<\/span><\/span><\/a><span class=\"EOP SCXW87226098 BCX0\" data-ccp-props=\"{\"335559685\":0}\"> <\/span><\/span><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-2dda7ed e-con-full fcol-panel e-flex e-con e-child\" data-id=\"2dda7ed\" data-element_type=\"container\" data-e-type=\"container\" id=\"spg50\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-b7085cf elementor-widget elementor-widget-heading\" data-id=\"b7085cf\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h3 class=\"elementor-heading-title elementor-size-default\">Hereditary spastic paraplegia type 50<\/h3>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-ed86c63 elementor-widget elementor-widget-heading\" data-id=\"ed86c63\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">Gene therapy using an AAV9 vector carrying the AP4M1 gene<\/p>\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-fb30d38 e-con-full e-flex e-con e-child\" data-id=\"fb30d38\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-037be59 e-con-full e-flex e-con e-child\" data-id=\"037be59\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-20a92a4 elementor-widget elementor-widget-heading\" data-id=\"20a92a4\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>Phase III<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-0b283bb elementor-widget elementor-widget-text-editor\" data-id=\"0b283bb\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">In the U.S. and Spain <\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-9456e48 e-con-full e-flex e-con e-child\" data-id=\"9456e48\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-378f81e elementor-widget elementor-widget-heading\" data-id=\"378f81e\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>Elpida Therapeutics \u2014 Program lead<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-69bb7af e-con-full e-flex e-con e-child\" data-id=\"69bb7af\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-7a48c0f elementor-widget elementor-widget-heading\" data-id=\"7a48c0f\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>16<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-9683ad2 elementor-widget elementor-widget-text-editor\" data-id=\"9683ad2\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\"><span class=\"TextRun SCXW256517898 BCX0\" lang=\"ES-ES\" data-contrast=\"auto\"><span class=\"NormalTextRun SCXW256517898 BCX0\">children treated (5 in Spain)<\/span><\/span><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-6c85ca5 e-con-full e-flex e-con e-child\" data-id=\"6c85ca5\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-ecfc0a7 elementor-widget elementor-widget-text-editor\" data-id=\"ecfc0a7\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\"><span class=\"TextRun SCXW194083533 BCX0\" lang=\"ES-ES\" data-contrast=\"auto\">SPG50 is a slowly progressive neurodegenerative disorder marked by global developmental delay, moderate to severe intellectual disability, impaired or absent speech, microcephaly, seizures, and progressive motor symptoms. Over time, muscle tone problems leave patients dependent on a wheelchair. This spasticity can extend to the upper limbs, which may lead to quadriplegia or the partial or total loss of use of all four limbs and the torso. <\/span><span class=\"LineBreakBlob BlobObject DragDrop SCXW194083533 BCX0\"><span class=\"SCXW194083533 BCX0\"> <\/span><br class=\"SCXW194083533 BCX0\"><\/span><span class=\"LineBreakBlob BlobObject DragDrop SCXW194083533 BCX0\"><span class=\"SCXW194083533 BCX0\"> <\/span><br class=\"SCXW194083533 BCX0\"><\/span><span class=\"TextRun SCXW194083533 BCX0\" lang=\"ES-ES\" data-contrast=\"none\"><span class=\"NormalTextRun SCXW194083533 BCX0\">There are no approved treatments to prevent, slow, or reverse the disease. <\/span><\/span><span class=\"TextRun SCXW194083533 BCX0\" lang=\"ES-ES\" data-contrast=\"auto\">Together with Elpida Therapeutics and Viralgen, we&#8217;re driving the development of Melpida, a gene therapy for SPG50. In April 2025, Hospital Sant Joan de D\u00e9u Barcelona (HSJD) and Fundaci\u00f3n Columbus signed a collaboration agreement to build an ecosystem of expert knowledge in advanced therapies for rare diseases in Spain. Thanks to this partnership, the first child under 3 with SPG50 was treated in Spain, opening the door to new hope for children across Europe with this disease.<\/span><span class=\"EOP SCXW194083533 BCX0\" data-ccp-props=\"{\"335559685\":0}\"> <\/span><\/p><p><strong>GOAL: \u20ac1,000,000 \u2014 DEADLINE 2028<\/strong><\/p><p>What it covers:<\/p><ul><li>Medical costs associated with Melpida treatment (surgical procedure, medical equipment, additional treatments, etc.)<\/li><li>Clinical follow-up for Alberto, Alejandro, Sergio, Ona, and Dani (medical visits, monitoring tests, clinical follow-up, consultations)<\/li><li>Melpida treatment for 4 new patients in Europe<\/li><li>FDA approval submission<\/li><li>Family support<\/li><\/ul>\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-7d8d06a e-con-full e-flex e-con e-child\" data-id=\"7d8d06a\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-b7ffd9c elementor-align-center elementor-mobile-align-left elementor-widget-mobile__width-inherit elementor-widget elementor-widget-button\" data-id=\"b7ffd9c\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/real-stories\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Discover real stories<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-59b8e9c elementor-align-center elementor-mobile-align-left elementor-widget elementor-widget-button\" data-id=\"59b8e9c\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/donate\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Support us<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-4baa65e elementor-widget elementor-widget-text-editor\" data-id=\"4baa65e\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\"><span class=\"TextRun SCXW83181901 BCX0\" lang=\"ES-ES\" data-contrast=\"auto\"><span class=\"NormalTextRun SCXW83181901 BCX0\">Source: <\/span><\/span><a class=\"Hyperlink SCXW83181901 BCX0\" href=\"https:\/\/pmc.ncbi.nlm.nih.gov\/articles\/PMC11271397\/\" target=\"_blank\" rel=\"noreferrer noopener\"><span class=\"TextRun Underlined SCXW83181901 BCX0\" lang=\"ES-ES\" data-contrast=\"none\"><span class=\"NormalTextRun SCXW83181901 BCX0\" data-ccp-charstyle=\"Hyperlink\">https:\/\/pmc.ncbi.nlm.nih.gov\/articles\/PMC11271397\/<\/span><\/span><\/a><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-e42cdc4 e-con-full fcol-panel e-flex e-con e-child\" data-id=\"e42cdc4\" data-element_type=\"container\" data-e-type=\"container\" id=\"ctnnb1\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-75f0eb8 elementor-widget elementor-widget-heading\" data-id=\"75f0eb8\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h3 class=\"elementor-heading-title elementor-size-default\">CTNNB1 syndrome<\/h3>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-61d5509 elementor-widget elementor-widget-heading\" data-id=\"61d5509\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">Gene therapy using an AAV9 vector carrying the CTNNB1 gene<\/p>\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-5cf2352 e-con-full e-flex e-con e-child\" data-id=\"5cf2352\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-a99ac86 e-con-full e-flex e-con e-child\" data-id=\"a99ac86\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-65d581e elementor-widget elementor-widget-heading\" data-id=\"65d581e\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>Phase I<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-c382ca4 elementor-widget elementor-widget-text-editor\" data-id=\"c382ca4\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">In Europe<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<a class=\"elementor-element elementor-element-8dba136 e-con-full e-flex e-con e-child\" data-id=\"8dba136\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\" href=\"https:\/\/asociacionctnnb1.org\/\" target=\"_blank\" rel=\"noopener\">\n\t\t\t\t<div class=\"elementor-element elementor-element-ceecd33 elementor-widget elementor-widget-heading\" data-id=\"ceecd33\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>CTNNB1 Foundation \u2014 Program lead<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<\/a>\n\t\t<div class=\"elementor-element elementor-element-f45539c e-con-full e-flex e-con e-child\" data-id=\"f45539c\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-1c23a67 elementor-widget elementor-widget-heading\" data-id=\"1c23a67\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">2<\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-0518e24 elementor-widget elementor-widget-text-editor\" data-id=\"0518e24\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p><span class=\"TextRun SCXW189189523 BCX0\" lang=\"ES-ES\" data-contrast=\"auto\"><span class=\"NormalTextRun SCXW189189523 BCX0\">children treated<\/span><\/span><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-f0c0a37 e-con-full e-flex e-con e-child\" data-id=\"f0c0a37\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-570859a elementor-widget elementor-widget-text-editor\" data-id=\"570859a\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>The CTNNB1 gene is the most common cause of misdiagnosed cerebral palsy. It&#8217;s a severe neurodevelopmental disorder caused by an alteration in the CTNNB1 gene. The syndrome is associated with developmental delay, intellectual disability, speech difficulties, motor difficulties, and behavioral disorders, including symptoms of autism and ADHD. There are no approved treatments to prevent, slow, or reverse the disease.<span data-ccp-props=\"{\"335559685\":0}\"> <\/span><\/p><p><span data-contrast=\"auto\">Together with the CTNNB1 Foundation, led by \u0160pela Mirosevic, the CTNNB1 Spain Association, and Viralgen Vector Core, we want to bring Urbagen to life: the world&#8217;s first gene replacement therapy for this disease.<\/span><span data-ccp-props=\"{\"335559685\":0}\"> <\/span><\/p><p><span data-contrast=\"auto\">Since then, we&#8217;ve been working together to treat the first patients in the first clinical trial, expected in late 2025 or early 2026.<\/span><span data-ccp-props=\"{\"335559685\":0}\"> <\/span><\/p><p><strong>GOAL: \u20ac750,000 \u2014 DEADLINE 2027<\/strong><\/p><ul><li>Treatment for 5 patients at Hospital Sant Joan de D\u00e9u<\/li><li>Medical costs associated with Urbagen treatment (surgical procedure, medical equipment, hospitalization, etc.)<\/li><li>Phase 1\/2 clinical trial costs (diagnostic tests, medical visits, clinical evaluations, etc.)<\/li><li>Post-treatment support therapies<\/li><li>Family support for travel and 6 months of accommodation during clinical follow-up<\/li><\/ul>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-c45ff73 e-con-full e-flex e-con e-child\" data-id=\"c45ff73\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-1c7a43d elementor-align-center elementor-mobile-align-left elementor-widget-mobile__width-inherit elementor-widget elementor-widget-button\" data-id=\"1c7a43d\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/real-stories\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Discover real stories<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-37d59cc elementor-align-center elementor-mobile-align-left elementor-widget elementor-widget-button\" data-id=\"37d59cc\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/donate\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Support us<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-25fd1e3 e-con-full fcol-panel e-flex e-con e-child\" data-id=\"25fd1e3\" data-element_type=\"container\" data-e-type=\"container\" id=\"cmt4j\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-db534ee elementor-widget elementor-widget-heading\" data-id=\"db534ee\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h3 class=\"elementor-heading-title elementor-size-default\">Charcot-Marie-Tooth disease type 4J<\/h3>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-85c9f4e elementor-widget elementor-widget-heading\" data-id=\"85c9f4e\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">Gene therapy using an AAV9 vector carrying the FIG4 gene <\/p>\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-7d684e3 e-con-full e-flex e-con e-child\" data-id=\"7d684e3\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-ec38bbb e-con-full e-flex e-con e-child\" data-id=\"ec38bbb\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-b2ea966 elementor-widget elementor-widget-heading\" data-id=\"b2ea966\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>Phase I<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-6731a14 elementor-widget elementor-widget-text-editor\" data-id=\"6731a14\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">Europe<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-1b3066c e-con-full e-flex e-con e-child\" data-id=\"1b3066c\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-33a4a9d elementor-widget elementor-widget-heading\" data-id=\"33a4a9d\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>0<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-21a80d5 elementor-widget elementor-widget-text-editor\" data-id=\"21a80d5\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\"><span class=\"TextRun SCXW54308011 BCX0\" lang=\"ES-ES\" data-contrast=\"none\"><span class=\"NormalTextRun SCXW54308011 BCX0\">children treated<\/span><\/span><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-5ee9ddf e-con-full e-flex e-con e-child\" data-id=\"5ee9ddf\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-5cb6fd6 elementor-widget elementor-widget-text-editor\" data-id=\"5cb6fd6\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>CMT4J is an inherited peripheral neuropathy caused by mutations in the FIG4 gene, causing progressive muscle weakness, loss of sensation, and respiratory failure. It&#8217;s frequently misdiagnosed as ALS or CIDP. The disease progresses steadily, compromising patients&#8217; mobility and independence. There are no approved treatments to prevent, slow, or reverse the disease.<\/p><p><span data-contrast=\"auto\">Together with Elpida Therapeutics, CMT Research Foundation, CureCMT4J, and Viralgen, we&#8217;ve funded the manufacturing of ELP-02, the first gene therapy for this disease. The first clinical trial begins in May 2026 in the U.S. <\/span> <\/p><p class=\"p1\">*This program is currently available only in the United States. Contact <a href=\"mailto:info@fundacioncolumbus.org\">info@fundacioncolumbus.org<\/a> for more information about the project. <\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-1a191af e-con-full e-flex e-con e-child\" data-id=\"1a191af\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-fad8dfa elementor-align-center elementor-mobile-align-left elementor-widget-mobile__width-inherit elementor-widget elementor-widget-button\" data-id=\"fad8dfa\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/real-stories\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Discover real stories<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-1eb6b76 elementor-align-center elementor-mobile-align-left elementor-widget elementor-widget-button\" data-id=\"1eb6b76\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/donate\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Support us<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-fe88b09 e-con-full fcol-panel e-flex e-con e-child\" data-id=\"fe88b09\" data-element_type=\"container\" data-e-type=\"container\" id=\"cln7\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-9356a10 elementor-widget elementor-widget-heading\" data-id=\"9356a10\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h3 class=\"elementor-heading-title elementor-size-default\">Neuronal ceroid lipofuscinosis type 7 (CLN7)\n<\/h3>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-6a2f6bd elementor-widget elementor-widget-heading\" data-id=\"6a2f6bd\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">Gene therapy using a self-complementary AAV9 vector (scAAV9) carrying the MFSD8 gene<\/p>\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-bafdc3d e-con-full e-flex e-con e-child\" data-id=\"bafdc3d\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-5a15286 e-con-full e-flex e-con e-child\" data-id=\"5a15286\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-5fea4d0 elementor-widget elementor-widget-heading\" data-id=\"5fea4d0\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>Phase I<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-7b1ba1c elementor-widget elementor-widget-text-editor\" data-id=\"7b1ba1c\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">In the U.S.<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-71a0284 e-con-full e-flex e-con e-child\" data-id=\"71a0284\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-992e3dc elementor-widget elementor-widget-heading\" data-id=\"992e3dc\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>Elpida Therapeutics \u2014 Program lead\n<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-fefa0c6 e-con-full e-flex e-con e-child\" data-id=\"fefa0c6\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-302bef5 elementor-widget elementor-widget-heading\" data-id=\"302bef5\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>4<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-e083b12 elementor-widget elementor-widget-text-editor\" data-id=\"e083b12\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">children treated<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-cd2ae29 e-con-full e-flex e-con e-child\" data-id=\"cd2ae29\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-1c8e668 elementor-widget elementor-widget-text-editor\" data-id=\"1c8e668\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p><span data-contrast=\"auto\">CLN7 is a lysosomal neurodegenerative disease and one of the rarest forms of Batten disease. It&#8217;s caused by mutations in the MFSD8 gene and leads to progressive vision loss, treatment-resistant seizures, and severe cognitive and motor decline. Onset typically occurs between ages 2 and 7. The disease progresses to a vegetative state and, generally, death in adolescence. There are currently no treatments to prevent, slow, or reverse the disease.    <\/span><span data-ccp-props=\"{\"134233117\":false,\"134233118\":false,\"201341983\":0,\"335551550\":1,\"335551620\":1,\"335559685\":0,\"335559737\":0,\"335559738\":0,\"335559739\":0,\"335559740\":259}\"> <\/span><\/p><p><span data-contrast=\"auto\">Together with Elpida Therapeutics, we&#8217;re working on the development of the first gene therapy for this disease. The first clinical trial is expected to begin in 2026 in the U.S. and Spain. <\/span><span data-ccp-props=\"{\"335559685\":0,\"335559739\":0}\"> <\/span><\/p><p><strong>GOAL: \u20ac550,000 \u2014 DEADLINE 2031<\/strong><\/p><ul><li>Treatment for 5 patients at Hospital Sant Joan de D\u00e9u<\/li><li>Medical costs associated with gene therapy (surgical procedure, medical equipment, hospitalization, etc.)<\/li><li>Phase 1\/2 clinical trial costs (diagnostic tests, medical visits, clinical evaluations, etc.)<\/li><li>Family support<\/li><\/ul>\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-141a92d e-con-full e-flex e-con e-child\" data-id=\"141a92d\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-e8f1144 elementor-align-center elementor-mobile-align-left elementor-widget-mobile__width-inherit elementor-widget elementor-widget-button\" data-id=\"e8f1144\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/real-stories\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Discover real stories<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-b812f04 elementor-align-center elementor-mobile-align-left elementor-widget elementor-widget-button\" data-id=\"b812f04\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/donate\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Support us<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-2f5a089 elementor-widget elementor-widget-text-editor\" data-id=\"2f5a089\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p><span class=\"TextRun SCXW170081357 BCX0\" lang=\"EN-US\" data-contrast=\"auto\"><span class=\"NormalTextRun SCXW170081357 BCX0\">Source:<\/span><\/span><span class=\"TextRun SCXW170081357 BCX0\" lang=\"EN-US\" data-contrast=\"none\"><span class=\"NormalTextRun SCXW170081357 BCX0\"> <\/span><\/span><a class=\"Hyperlink SCXW170081357 BCX0\" href=\"https:\/\/pubmed.ncbi.nlm.nih.gov\/41314141\/\" target=\"_blank\" rel=\"noreferrer noopener\"><span class=\"TextRun Underlined SCXW170081357 BCX0\" lang=\"EN-US\" data-contrast=\"none\"><span class=\"NormalTextRun SCXW170081357 BCX0\" data-ccp-charstyle=\"Hyperlink\">https:\/\/pubmed.ncbi.nlm.nih.gov\/41314141\/<\/span><\/span><\/a><span class=\"EOP SCXW170081357 BCX0\" data-ccp-props=\"{\"134233117\":false,\"134233118\":false,\"201341983\":0,\"335551550\":1,\"335551620\":1,\"335559685\":0,\"335559737\":0,\"335559738\":0,\"335559739\":0,\"335559740\":259}\"> <\/span><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-23480f5 e-con-full fcol-panel e-flex e-con e-child\" data-id=\"23480f5\" data-element_type=\"container\" data-e-type=\"container\" id=\"more\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-8af0fa2 elementor-widget elementor-widget-heading\" data-id=\"8af0fa2\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h2 class=\"elementor-heading-title elementor-size-default\">More diseases, more answers<\/h2>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-1635c91 elementor-widget elementor-widget-text-editor\" data-id=\"1635c91\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\"><span class=\"TextRun SCXW23359612 BCX0\" lang=\"ES-ES\" data-contrast=\"auto\">Goal 10 goes beyond our active programs. Before adding a new disease, we assess its scientific viability: an identified gene, an estimated patient population, a viable AAV vector, and an organized patient community. Lafora disease is next on our list.<\/span><span class=\"LineBreakBlob BlobObject DragDrop SCXW23359612 BCX0\"><span class=\"SCXW23359612 BCX0\"> <\/span><br class=\"SCXW23359612 BCX0\"><\/span><\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-d4224b5 elementor-widget elementor-widget-text-editor\" data-id=\"d4224b5\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p class=\"p1\">Researching a disease that fits our focus?<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-cde8f35 elementor-align-left elementor-mobile-align-left elementor-widget-mobile__width-initial elementor-widget elementor-widget-button\" data-id=\"cde8f35\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"button.default\">\n\t\t\t\t\t\t\t\t\t\t<a class=\"elementor-button elementor-button-link elementor-size-sm\" href=\"https:\/\/fundacioncolumbus.org\/en\/contact\/\">\n\t\t\t\t\t\t<span class=\"elementor-button-content-wrapper\">\n\t\t\t\t\t\t\t\t\t<span class=\"elementor-button-text\">Get in touch<\/span>\n\t\t\t\t\t<\/span>\n\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-1dfd9a5 elementor-widget elementor-widget-html\" data-id=\"1dfd9a5\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"html.default\">\n\t\t\t\t\t<script>document.addEventListener(\"DOMContentLoaded\", function () {\n  const tabs = document.querySelectorAll(\".fcol-tab\");\n  const panels = document.querySelectorAll(\".fcol-panel\");\n\n  tabs.forEach((tab) => {\n    tab.addEventListener(\"click\", function (e) {\n      e.preventDefault();\n\n      const target = this.dataset.tab;\n\n      tabs.forEach((item) => item.classList.remove(\"is-active\"));\n      panels.forEach((panel) => panel.classList.remove(\"is-active\"));\n\n      this.classList.add(\"is-active\");\n\n      if (!target) return;\n\n      const targetPanel = document.getElementById(target);\n      if (targetPanel) {\n        targetPanel.classList.add(\"is-active\");\n      }\n    });\n  });\n});\n<\/script>\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-c24d29a e-flex e-con-boxed e-con e-parent\" data-id=\"c24d29a\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t\t<div class=\"e-con-inner\">\n\t\t\t\t<div class=\"elementor-element elementor-element-4768b5c elementor-widget elementor-widget-heading\" data-id=\"4768b5c\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h2 class=\"elementor-heading-title elementor-size-default\">Advancing the therapies we drive forward<\/h2>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-9d5ec9e elementor-widget elementor-widget-image\" data-id=\"9d5ec9e\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"800\" height=\"291\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/05\/Grafico-Pipeline-2-1024x372.webp\" class=\"attachment-large size-large wp-image-18773\" alt=\"\" srcset=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/05\/Grafico-Pipeline-2-1024x372.webp 1024w, https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/05\/Grafico-Pipeline-2-300x109.webp 300w, https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/05\/Grafico-Pipeline-2-768x279.webp 768w, https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/05\/Grafico-Pipeline-2-1536x558.webp 1536w, https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/05\/Grafico-Pipeline-2-2048x744.webp 2048w\" sizes=\"(max-width: 800px) 100vw, 800px\" \/>\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-8ebf178 elementor-widget elementor-widget-image\" data-id=\"8ebf178\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"980\" height=\"105\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/SECUENCIA-DECORATIVA-ICONOS-LOW.svg\" class=\"attachment-large size-large wp-image-18771\" alt=\"\" \/>\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-c1d4da3 e-flex e-con-boxed e-con e-parent\" data-id=\"c1d4da3\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t\t<div class=\"e-con-inner\">\n\t\t\t\t<div class=\"elementor-element elementor-element-ecfe7d8 elementor-widget elementor-widget-heading\" data-id=\"ecfe7d8\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h2 class=\"elementor-heading-title elementor-size-default\">Advancing science where others don't reach<\/h2>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-7c7e19d elementor-widget elementor-widget-text-editor\" data-id=\"7c7e19d\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>We drive scientific innovation around the world, wherever it&#8217;s needed most, connecting researchers, institutions, and biotech companies to accelerate the development of therapies that would otherwise take decades to arrive. We also act as an amplifier: we raise awareness, build bridges, and make visible what science is achieving. <\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-d9aee9a e-con-full e-flex e-con e-child\" data-id=\"d9aee9a\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-739782e e-con-full e-flex e-con e-child\" data-id=\"739782e\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-1073da7 elementor-widget elementor-widget-heading\" data-id=\"1073da7\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>6<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-9bc9c9f elementor-widget elementor-widget-text-editor\" data-id=\"9bc9c9f\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Active research projects<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-12b1298 e-con-full e-flex e-con e-child\" data-id=\"12b1298\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-5559788 elementor-widget elementor-widget-heading\" data-id=\"5559788\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>+<\/span><span>20<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-2c79ade elementor-widget elementor-widget-text-editor\" data-id=\"2c79ade\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Institutional partnerships<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-4ad8807 e-con-full e-flex e-con e-child\" data-id=\"4ad8807\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-1ea03c0 elementor-widget elementor-widget-heading\" data-id=\"1ea03c0\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>1<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-d7ed4df elementor-widget elementor-widget-text-editor\" data-id=\"d7ed4df\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Active international consortium<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-35ced4c e-con-full e-flex e-con e-child\" data-id=\"35ced4c\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-7e44aa0 elementor-widget__width-initial elementor-widget elementor-widget-text-editor\" data-id=\"7e44aa0\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<span style=\"font-weight: 600;\">Are you a researcher or scientific institution?<\/span><br><span style=\"font-weight: 800;\">Tell us about your project<\/span>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-d6f260d elementor-widget elementor-widget-image\" data-id=\"d6f260d\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<a href=\"https:\/\/fundacioncolumbus.org\/en\/contact\/\">\n\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"315\" height=\"258\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/03\/Flecha-Azul-marino.svg\" class=\"attachment-large size-large wp-image-18778\" alt=\"\" \/>\t\t\t\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-01e7551 e-con-full e-flex e-con e-parent\" data-id=\"01e7551\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t\t\t<div class=\"elementor-element elementor-element-605b368 elementor-widget elementor-widget-image-carousel\" data-id=\"605b368\" data-element_type=\"widget\" data-e-type=\"widget\" data-settings=\"{&quot;slides_to_show&quot;:&quot;8&quot;,&quot;slides_to_show_tablet&quot;:&quot;4&quot;,&quot;slides_to_show_mobile&quot;:&quot;2&quot;,&quot;slides_to_scroll&quot;:&quot;1&quot;,&quot;navigation&quot;:&quot;none&quot;,&quot;autoplay_speed&quot;:0,&quot;speed&quot;:5000,&quot;image_spacing_custom&quot;:{&quot;unit&quot;:&quot;px&quot;,&quot;size&quot;:60,&quot;sizes&quot;:[]},&quot;autoplay&quot;:&quot;yes&quot;,&quot;pause_on_hover&quot;:&quot;yes&quot;,&quot;infinite&quot;:&quot;yes&quot;,&quot;image_spacing_custom_tablet_extra&quot;:{&quot;unit&quot;:&quot;px&quot;,&quot;size&quot;:&quot;&quot;,&quot;sizes&quot;:[]},&quot;image_spacing_custom_tablet&quot;:{&quot;unit&quot;:&quot;px&quot;,&quot;size&quot;:&quot;&quot;,&quot;sizes&quot;:[]},&quot;image_spacing_custom_mobile&quot;:{&quot;unit&quot;:&quot;px&quot;,&quot;size&quot;:&quot;&quot;,&quot;sizes&quot;:[]}}\" data-widget_type=\"image-carousel.default\">\n\t\t\t\t\t\t\t<div class=\"elementor-image-carousel-wrapper swiper\" role=\"region\" aria-roledescription=\"carousel\" aria-label=\"Carrusel de im\u00e1genes\" dir=\"ltr\">\n\t\t\t<div class=\"elementor-image-carousel swiper-wrapper\" aria-live=\"off\">\n\t\t\t\t\t\t\t\t<div class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" aria-label=\"1 of 13\"><figure class=\"swiper-slide-inner\"><img decoding=\"async\" class=\"swiper-slide-image\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/Logo-SJD-Color-scaled.png\" alt=\"Logo SJD-Color\" \/><\/figure><\/div><div class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" aria-label=\"2 of 13\"><figure class=\"swiper-slide-inner\"><img decoding=\"async\" class=\"swiper-slide-image\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/Elpida_tx_logo-300x123-1.png\" alt=\"Elpida_tx_logo-300x123\" \/><\/figure><\/div><div class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" 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class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" aria-label=\"6 of 13\"><figure class=\"swiper-slide-inner\"><img decoding=\"async\" class=\"swiper-slide-image\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/Logo-Euterpe_Logo-negro-300x113-1.png\" alt=\"Logo-Euterpe_Logo-negro-300x113\" \/><\/figure><\/div><div class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" aria-label=\"7 of 13\"><figure class=\"swiper-slide-inner\"><img decoding=\"async\" class=\"swiper-slide-image\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/GRADOCELL_logo_web-2-300x131-1.png\" alt=\"GRADOCELL_logo_web-2-300x131\" \/><\/figure><\/div><div class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" aria-label=\"8 of 13\"><figure class=\"swiper-slide-inner\"><img decoding=\"async\" class=\"swiper-slide-image\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/Global_omnium_logo_erb-300x131-1.png\" alt=\"Global_omnium_logo_erb-300x131\" \/><\/figure><\/div><div class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" aria-label=\"9 of 13\"><figure class=\"swiper-slide-inner\"><img decoding=\"async\" class=\"swiper-slide-image\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/C.-VENTURE-PARTNERS-horizontal-negro-color-300x98-1.png\" alt=\"C.-VENTURE-PARTNERS-horizontal-negro-color-300x98\" \/><\/figure><\/div><div class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" aria-label=\"10 of 13\"><figure class=\"swiper-slide-inner\"><img decoding=\"async\" class=\"swiper-slide-image\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/bizkaiko-foru-aldundia-diputacion-foral-logo-vector-300x152-1.png\" alt=\"bizkaiko-foru-aldundia-diputacion-foral-logo-vector-300x152\" \/><\/figure><\/div><div class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" aria-label=\"11 of 13\"><figure class=\"swiper-slide-inner\"><img decoding=\"async\" class=\"swiper-slide-image\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/Bilbao_Udala_Ayuntamiento_logo-300x188-1.png\" alt=\"Bilbao_Udala_Ayuntamiento_logo-300x188\" \/><\/figure><\/div><div class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" aria-label=\"12 of 13\"><figure class=\"swiper-slide-inner\"><img decoding=\"async\" class=\"swiper-slide-image\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/AsjBio-300x91-1.png\" alt=\"AsjBio-300x91\" \/><\/figure><\/div><div class=\"swiper-slide\" role=\"group\" aria-roledescription=\"slide\" aria-label=\"13 of 13\"><figure class=\"swiper-slide-inner\"><img decoding=\"async\" class=\"swiper-slide-image\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/04\/ALBIAN-Group-300x131-1.png\" alt=\"ALBIAN-Group-300x131\" \/><\/figure><\/div>\t\t\t<\/div>\n\t\t\t\t\t\t\t\n\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-2e453c8 e-flex e-con-boxed e-con e-parent\" data-id=\"2e453c8\" data-element_type=\"container\" data-e-type=\"container\" id=\"cultura\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t\t<div class=\"e-con-inner\">\n\t\t\t\t<div class=\"elementor-element elementor-element-640174c elementor-widget elementor-widget-heading\" data-id=\"640174c\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\">CULTURE<\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-579b364 elementor-widget elementor-widget-heading\" data-id=\"579b364\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h2 class=\"elementor-heading-title elementor-size-default\">Culture that drives visibility for our mission<\/h2>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-b62d999 elementor-widget elementor-widget-text-editor\" data-id=\"b62d999\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Every concert, every festival, every fundraising event we organize has one clear purpose: funding access to therapy for children with ultra-rare diseases. Culture lets us reach more people, build awareness, and turn that support into real access. <\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-8955ca6 e-con-full e-flex e-con e-child\" data-id=\"8955ca6\" data-element_type=\"container\" data-e-type=\"container\">\n\t\t<div class=\"elementor-element elementor-element-efb6481 e-con-full e-flex e-con e-child\" data-id=\"efb6481\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-a844307 elementor-widget elementor-widget-heading\" data-id=\"a844307\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>+<\/span><span>70<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-82aa5c6 elementor-widget-mobile__width-initial elementor-widget elementor-widget-text-editor\" data-id=\"82aa5c6\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Cultural, scientific, and sporting fundraising events<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-71e9a64 e-con-full e-flex e-con e-child\" data-id=\"71e9a64\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-bb64196 elementor-widget elementor-widget-heading\" data-id=\"bb64196\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>5<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-7e2aaca elementor-widget elementor-widget-text-editor\" data-id=\"7e2aaca\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Editions of our charity festival<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-a18526f elementor-widget elementor-widget-image\" data-id=\"a18526f\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"753\" height=\"224\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/03\/Logo-Festival-RenHacer-Blanco-1.svg\" class=\"attachment-large size-large wp-image-18781\" alt=\"\" \/>\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-b5cdadd e-con-full e-flex e-con e-child\" data-id=\"b5cdadd\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t<div class=\"elementor-element elementor-element-ce3b52e elementor-widget elementor-widget-heading\" data-id=\"ce3b52e\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<p class=\"elementor-heading-title elementor-size-default\"><span>+<\/span><span>15<\/span><\/p>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-4935b19 elementor-widget-mobile__width-initial elementor-widget elementor-widget-text-editor\" data-id=\"4935b19\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Cities reached through our events<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t<div class=\"elementor-element elementor-element-53e44c6 e-flex e-con-boxed e-con e-parent\" data-id=\"53e44c6\" data-element_type=\"container\" data-e-type=\"container\" data-settings=\"{&quot;background_background&quot;:&quot;classic&quot;}\">\n\t\t\t\t\t<div class=\"e-con-inner\">\n\t\t\t\t<div class=\"elementor-element elementor-element-093c831 elementor-widget elementor-widget-heading\" data-id=\"093c831\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"heading.default\">\n\t\t\t\t\t<h2 class=\"elementor-heading-title elementor-size-default\">There\u2019s no better plan than helping<\/h2>\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-c713d56 elementor-widget elementor-widget-image\" data-id=\"c713d56\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"image.default\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"753\" height=\"169\" src=\"https:\/\/fundacioncolumbus.org\/wp-content\/uploads\/2026\/03\/Logo-Festival-RenHacer-Azul-1.svg\" class=\"attachment-large size-large wp-image-18703\" alt=\"\" \/>\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-10f6360 elementor-widget-tablet__width-initial elementor-widget elementor-widget-text-editor\" data-id=\"10f6360\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>The 5th RenHacer Festival comes to Oviedo on May 30 and Arantzazu on June 13. Proceeds will fund the launch of the Phase 1\/2 clinical trial for CTNNB1 syndrome at Hospital Sant Joan de D\u00e9u. One ticket, one step closer to <a href=\"https:\/\/fundacioncolumbus.org\/en\/real-stories\/#urban\">Urbagen<\/a>.  <\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<div class=\"elementor-element elementor-element-18059a4 elementor-widget elementor-widget-text-editor\" data-id=\"18059a4\" data-element_type=\"widget\" data-e-type=\"widget\" data-widget_type=\"text-editor.default\">\n\t\t\t\t\t\t\t\t\t<p>Since 2017, every step forward has been possible thanks to those who believed in it.<\/p>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t","protected":false},"excerpt":{"rendered":"<p>Accelerating access to advanced therapies for children with ultra-rare diseases Our vision: no child left without treatment Treating an ultra-rare disease takes more than science. It takes coordination, sustained funding, strategic partnerships, and the involvement of society as a whole. People Innovation Culture PEOPLE Advanced therapies for those who need them most The burden of [&hellip;]<\/p>\n","protected":false},"author":2,"featured_media":18769,"parent":0,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"elementor_header_footer","meta":{"give_campaign_id":0,"footnotes":""},"class_list":["post-18762","page","type-page","status-publish","has-post-thumbnail","hentry"],"campaignId":"","_links":{"self":[{"href":"https:\/\/fundacioncolumbus.org\/en\/wp-json\/wp\/v2\/pages\/18762","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/fundacioncolumbus.org\/en\/wp-json\/wp\/v2\/pages"}],"about":[{"href":"https:\/\/fundacioncolumbus.org\/en\/wp-json\/wp\/v2\/types\/page"}],"author":[{"embeddable":true,"href":"https:\/\/fundacioncolumbus.org\/en\/wp-json\/wp\/v2\/users\/2"}],"replies":[{"embeddable":true,"href":"https:\/\/fundacioncolumbus.org\/en\/wp-json\/wp\/v2\/comments?post=18762"}],"version-history":[{"count":12,"href":"https:\/\/fundacioncolumbus.org\/en\/wp-json\/wp\/v2\/pages\/18762\/revisions"}],"predecessor-version":[{"id":18934,"href":"https:\/\/fundacioncolumbus.org\/en\/wp-json\/wp\/v2\/pages\/18762\/revisions\/18934"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/fundacioncolumbus.org\/en\/wp-json\/wp\/v2\/media\/18769"}],"wp:attachment":[{"href":"https:\/\/fundacioncolumbus.org\/en\/wp-json\/wp\/v2\/media?parent=18762"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}